New cell experiments show more effective genetic 'cuts' that could one day become the foundation of more effective gene therapies.
List view / Grid view
Filter the results
Genomics is the branch of molecular biology concerned with the structure, function, evolution, and mapping of genomes.
An AAV-delivered gene therapy has demonstrated success in animal models of temporal lobe epilepsy, so could be a therapeutic option for human patients.
A study has revealed that in rhesus monkeys, a genetic mutation could be the cause of Bardet-Biedl Syndrome, providing a way to study the disease and develop therapies.
A new antiviral drug has been reported in a study that researchers believe has high clinical potential as a next-generation influenza drug.
Researchers have discovered a gene in zebrafish that enables them to successfully recover after cardiac damage, which could be used to repair heart tissues in humans.
Mouse blastocyst-like structures called blastoids have been developed by a team which could be used to study early developmental diseases.
Whole exome sequencing has been used by researchers to reveal 10 genes implicated in the development of schizophrenia.
A study has demonstrated how to use CRISPR to deliver DNA to particular bacteria, which could be used as an alternative to antibiotics.
A study has revealed that a mutation in the NKAP gene causes a rare syndrome, providing researchers with the potential to develop treatments for the condition.
New research provides insights into how cancers can arise when DNA polymerase delta is not functioning properly.
A study has demonstrated that blocking certain receptors in mice reduced Ewing sarcoma growth and metastasis, which could be used within future treatments.
The newly identified variant could play a role in gene therapies that require high accuracy and precision.
These findings highlight the complexity of the relationship between genes and human brain function.
Researchers have used whole genome sequencing to analyse breast cancers and reveal which are more responsive to treatments, which could improve the development of oncologic therapies.