By targeting a previously undiscovered allosteric site on a DMD-associated enzyme, researchers found muscle cell conditions improved.
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Duchenne muscular dystrophy (DMD)
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Researchers capitalised on novel sequencing technologies to produce the first end-to-end DNA sequence of the X chromosome.
Researchers have created an accurate mouse model of Duchenne muscular dystrophy (DMD), showing that TGFβ is a potential target for the condition.
Upregulating utrophin using small molecules could be a new therapeutic approach for Duchenne muscular dystrophy (DMD).
Gene therapy for the treatment of Duchenne muscular dystrophy has safely stopped the muscle deterioration associated with the disease.
A study has revealed that using DNA-like molecules to repair gene mutations in models could act as a successful therapy for patients.
Breakthrough research has uncovered an unexpected mechanism that underlies cardiomyopathy in DMD...
A protein known to drive nerve cell survival in the brain and spinal cord may also protect failing hearts in children and young adults with DMD...
Scientists have developed a CRISPR gene-editing technique that can potentially correct a majority of mutations that cause DMD...